Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study

About

Brief Summary

This project is a global, multicenter, prospective, longitudinal, observational natural history study that can be used to understand the disease progression and support the development of safe and effective drugs and biological products for Friedreich ataxia.

Study Type

Observational

Eligibility

Gender

All

Healthy Volunteers

Yes

Minimum Age

N/A

Maximum Age

N/A

Inclusion Criteria:

Both males and females of any age
Individuals with Friedreich ataxia (FA): Participants that meet genetically confirmed diagnosis of Friedreich ataxia
Written informed consent provided
- Informed consent must be obtained for all participants
- For underage participants, they and the parent/ legally authorized representative have to sign the informed consent form, child assent (if applicable)
- Persons who are not legally competent require the informed consent of their legally authorized representative Exclusion Criteria:
Unable or unwilling to provide informed consent
Acute or ongoing medical or other conditions that would interfere with the conduct and assessments of the study
For any reason in the opinion of the investigator, participant would be unlikely or unable to comply with study protocol requirements.